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Zevra’s Miplyffa Wins First-Ever US Approval, But In Combination With Off-Label Miglustat

Drug’s List Price Is $1m Per Year On Average

Executive Summary

Miplyffa (arimoclomol) was approved for Niemann-Pick disease type C when administered with another high-priced drug used off label as standard of care for about 80% of NPC patients. 

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