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Alnylam's Fitusiran Could Provide Comprehensive Hemophilia Therapy Option

Executive Summary

Fitusiran's mechanism of reducing antithrombin levels could apply to all hemophilia patients, as well as those with other rare bleeding disorders. Reducing antithrombin increases thrombin levels and helps to increase normal clotting.

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Alnylam Hopes To Resume Fitusiran Dosing Quickly, Despite Unclear Cause Of Trial Death

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Alnylam's Overshadowed Givosiran Comes Into The Phase III Light

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